News and Innovation
What is changing in clinical research — AI and digital tools, gene therapy and biotech, new trial models, and treatment advances in specific conditions. Written to explain why a development matters, not just to report that it happened.
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When Scleroderma Defies the Usual Medical Playbook
Read more: When Scleroderma Defies the Usual Medical PlaybookCorrects the myth that scleroderma is just a skin disease, walking through systemic sclerosis’s multi-organ effects, key tests, layered treatments, and why…
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Advances in Rare Bleeding Disorder Treatments
Read more: Advances in Rare Bleeding Disorder TreatmentsReviews how gene therapy, rebalancing agents, and international clinical trials are moving care for Factor XI deficiency and other rare bleeding disorders…
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New Therapies Reshaping Duchenne Expectations
Read more: New Therapies Reshaping Duchenne ExpectationsRewritten Aug 2026. Opens in the car after the diagnosis, then explains in plain language why the science has shifted to the…
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Understanding Haemophilia Beyond the Basics
Read more: Understanding Haemophilia Beyond the BasicsRewritten Aug 2026. Opens with a child’s bump at the park, then covers day-to-day life with haemophilia across ages, joint protection and…
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Living Well with Von Willebrand Disease
Read more: Living Well with Von Willebrand DiseaseReassuring update for people with von Willebrand disease on the changing treatment landscape, including recombinant factor products, longer-acting therapies, gene therapy research,…
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Immune Thrombocytopenia, or ITP, Beyond the Usual Conversations
Read more: Immune Thrombocytopenia, or ITP, Beyond the Usual ConversationsExplains ITP beyond the basics, covering the shift away from long-term steroids toward TPO receptor agonists and other modern therapies, and how…
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Acute Promyelocytic Leukaemia and the Race Against Time
Read more: Acute Promyelocytic Leukaemia and the Race Against TimeExplains why APL is a medical emergency needing immediate targeted treatment, how ATRA and arsenic trioxide transformed outcomes, and how patients can…
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Acute Myeloid Leukemia: Finding Options When Treatment Stops Working
Read more: Acute Myeloid Leukemia: Finding Options When Treatment Stops WorkingExplains relapsed vs refractory AML, walks through next-step treatment options from salvage chemotherapy to stem cell transplant, and shows how specialist centers…
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Considering Gene Editing As A Personal Treatment Path
Read more: Considering Gene Editing As A Personal Treatment PathA patient-focused explainer on gene editing for rare diseases, covering how it differs from gene therapy, its benefits and risks, paid trial…
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Biotech Driven Studies and What Patients Should Know
Read more: Biotech Driven Studies and What Patients Should KnowExplains what biotech-sponsored clinical trials are, how they differ from traditional academic studies, and how trialport helps patients find and understand nearby…